Spark Therapeutics, Inc. is a leading gene therapy company based in Philadelphia, PA. They are dedicated to unlocking the potential of gene therapy to revolutionize healthcare by developing innovative treatments for patients with inherited diseases, including inherited retinal diseases, liver-directed diseases such as hemophilia, and neurodegenerative diseases. With their cutting-edge vector design, state-of-the-art manufacturing expertise, and strong commitment to improving patient care, Spark Therapeutics is at the forefront of gene therapy innovation.
Spark Therapeutics is known for their fully integrated approach, combining their proprietary adeno-associated viral (AAV) gene therapy platform with excellence in research and development, manufacturing, and commercial operations. Their mission is to accelerate healthcare transformation by turning genes into medicines, and they are committed to collaborating with cross-functional teams and partners to realize the full potential of gene therapy. With their proposed Gene Therapy Innovation Center in West Philadelphia, Spark Therapeutics aims to bring together the greatest minds in gene therapy under one roof, further advancing their groundbreaking work and sparking change in the local community.
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